MGTX MeiraGTx Holdings plc - Ordinary Shares
MGTX Stock Snapshot Price, market cap, P/E, EPS, ROE, debt/equity, 52-week range
MGTX Stock Price Chart Daily OHLCV with technical indicators — pan, zoom, and customize your view
10-Year Performance Revenue, net income, margins and EPS trends
Valuation P/E, P/S, P/B, EV/EBITDA ratios — is the stock expensive or cheap?
Profitability Gross, operating and net margins; ROE, ROA, ROIC
Financial Health Debt, liquidity, solvency — balance sheet strength
Growth Revenue, EPS and net income growth: YoY, 3Y CAGR, 5Y CAGR
Capital Efficiency Asset turnover, inventory turnover, receivables turnover
MGTX Analyst Consensus Bullish and bearish analyst opinions, 12-month price target, upside
- Strong Buy 4 30.8%
- Buy 8 61.5%
- Hold 1 7.7%
- Sell 0 0.0%
- Strong Sell 0 0.0%
12-Month Price Target
7 analysts · 2026-08-15Earnings History EPS actual vs estimate, surprise %, beat rate, next earnings date
| Period | EPS Actual | EPS Est | Surprise |
|---|---|---|---|
| March 31, 2026 | $-0.57 | $-0.41 | -0.16% |
| Dec. 31, 2025 | $0.19 | $-0.58 | 0.77% |
| Sept. 30, 2025 | $-0.62 | $-0.50 | -0.12% |
| June 30, 2025 | $-0.48 | $-0.48 | -0.00% |
| March 31, 2025 | $-0.51 | $-0.50 | -0.01% |
| Dec. 31, 2024 | $-0.50 | $-0.57 | 0.07% |
Peer comparison (GICS sub-industry) Key metrics vs sector peers
| Ticker | Market Cap | P/E | Rev YoY | Net Margin | ROE | Gross Margin |
|---|---|---|---|---|---|---|
| MGTX | $645M | -5.6 | 144.6% | -140.3% | 8062.2% | — |
| AKTS | — | — | — | — | — | — |
| CGEM | $624M | -3.2 | — | — | -44.0% | — |
| NVAX | $1.09B | 2.6 | 64.7% | 39.2% | -977.1% | — |
| INBX | $1.15B | -8.7 | 550.0% | -10773.5% | -365.9% | — |
| GLUE | $1.03B | — | 63.5% | -31.2% | -15.4% | — |
| CRVS | $575M | -14.5 | — | — | -21.6% | — |
| MNKD | $1.75B | 283.5 | 22.2% | 1.7% | -11.1% | — |
| REPL | $633M | -2.3 | — | — | -146.2% | — |
| VOR | $506M | -0.2 | — | — | 83.4% | — |
Full Fundamentals All metrics by year — income statement, balance sheet, cash flow
Income Statement 15
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Revenue | $81M | $33M | $14M | $16M | $38M | $16M | $13M | |
| R&D Expense | $130M | $119M | $104M | $86M | $67M | $34M | $25M | |
| SG&A Expense | $53M | $54M | $47M | $47M | $44M | $44M | $47M | |
| Operating Expenses | $187M | $197M | $151M | $132M | $110M | $78M | $72M | |
| Operating Income | $-106M | $-164M | $-137M | $-116M | $-73M | $-63M | $-58M | |
| Interest Expense | $12M | $13M | $13M | $5M | $288.0K | $139.0K | $48.6K | |
| Interest Income | $2M | $4M | $2M | $777.0K | $212.0K | $1M | $370.6K | |
| Pretax Income | $-114M | $-148M | $-84M | $-130M | $-80M | $-58M | $-55M | |
| Income Tax | $0 | $0 | $0 | $0 | $0 | $0 | $0 | |
| Net Income | $-114M | $-148M | $-84M | $-130M | $-80M | $-58M | $-55M | |
| EPS (Basic) | $-1.42 | $-2.12 | $-1.49 | $-2.87 | $-1.80 | $-1.54 | · | |
| EPS (Diluted) | $-1.42 | $-2.12 | $-1.49 | $-2.87 | $-1.80 | $-1.54 | · | |
| Shares (Basic) | 80,430,186 | 69,822,353 | 56,486,525 | 45,177,857 | 44,139,655 | 37,724,189 | · | |
| Shares (Diluted) | 80,430,186 | 69,822,353 | 56,486,525 | 45,177,857 | 44,139,655 | 37,724,189 | · | |
| EBITDA | $-93M | $-151M | $-123M | $-108M | $-65M | $-58M | $-58M |
Balance Sheet 27
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Cash & Equivalents | $66M | $104M | $130M | $116M | $138M | $210M | $227M | |
| Receivables | $3M | $707.0K | $10M | $21M | · | · | · | |
| Inventory | · | $385.0K | · | · | · | · | · | |
| Prepaid Expense | $6M | $7M | $6M | $8M | $8M | $7M | $4M | |
| Other Current Assets | $2M | $2M | $1M | $2M | $2M | $5M | $2M | |
| Current Assets | $92M | $124M | $160M | $154M | $183M | $273M | $269M | |
| PP&E (Net) | $105M | $103M | $116M | $109M | $76M | $44M | $24M | |
| PP&E (Gross) | $158M | $145M | $149M | $130M | $90M | $52M | $28M | |
| Accum. Depreciation | $53M | $42M | $33M | $20M | $14M | $8M | $5M | |
| Intangibles | $578.0K | $821.0K | $1M | $1M | $2M | $2M | · | |
| Other Non-current Assets | $1M | $1M | $2M | $1M | $1M | $1M | $195.1K | |
| Total Assets | $244M | $270M | $327M | $318M | $320M | $364M | $324M | |
| Accounts Payable | $10M | $24M | $16M | $17M | $15M | $7M | $4M | |
| Accrued Liabilities | $33M | $27M | $43M | $40M | $28M | $21M | $18M | |
| Short-term Debt | $25M | · | · | · | · | · | · | |
| Current Liabilities | $123M | $61M | $67M | $82M | $68M | $54M | $49M | |
| Capital Leases | $11M | $8M | $13M | $17M | $20M | $20M | $22M | |
| Deferred Tax | · | · | · | $186.0K | $196.0K | $214.0K | $195.1K | |
| Total Liabilities | $250M | $202M | $189M | $200M | $135M | $125M | $133M | |
| Total Debt | $25M | · | · | · | · | · | · | |
| Common Stock | $3.0K | $3.0K | $2.0K | $2.0K | $2.0K | $2.0K | $1.4K | |
| Paid-in Capital | $808M | $774M | $694M | $582M | $529M | $504M | $396M | |
| Retained Earnings | $-816M | $-702M | $-554M | $-470M | $-341M | $-261M | $-203M | |
| AOCI | $2M | $-4M | $-1M | $6M | $-3M | $-5M | $-2M | |
| Stockholders' Equity | $-6M | $68M | $138M | $118M | $185M | $239M | $191M | |
| Liabilities + Equity | $244M | $270M | $327M | $318M | $320M | $364M | $324M | |
| Shares Outstanding | 81,120,931 | 78,397,380 | 63,601,015 | 48,477,209 | 44,548,925 | 44,189,150 | 36,791,906 |
Cash Flow 14
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| D&A | $13M | $13M | $14M | $9M | $8M | $4M | $2M | |
| Stock-based Comp | $22M | $25M | $28M | $29M | $21M | $18M | $16M | |
| Deferred Tax | $-21M | $-24M | $-10M | $-26M | $-37M | $-16M | $-10M | |
| Amort. of Intangibles | · | · | · | $200.0K | $300.0K | $20.0K | $0 | |
| Other Non-cash | $54M | $29M | $-53M | $45M | $77M | $-13M | · | |
| Operating Cash Flow | $-46M | $-104M | $-105M | $-73M | $-11M | $-64M | $20M | |
| CapEx | $4M | $5M | $20M | $45M | $46M | $21M | $9M | |
| Investing Cash Flow | $-4M | $23M | $34M | $-45M | $-62M | $-37M | $-9M | |
| Stock Issued | $15M | $59M | $92M | $25M | · | $87M | $155M | |
| Net Stock Activity | $15M | $59M | $92M | · | · | $87M | $155M | |
| Financing Cash Flow | $12M | $55M | $84M | $95M | $2M | $83M | $148M | |
| Taxes Paid | $0 | $0 | · | · | · | · | · | |
| Free Cash Flow | $-50M | $-109M | $-126M | $-118M | $-57M | $-85M | $11M | |
| Levered FCF | $-62M | $-123M | · | $-123M | $-57M | $-85M | · |
Profitability 7
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Operating Margin | -130.2% | -493.4% | · | -730.9% | -194.1% | -401.9% | -438.4% | |
| Net Margin | -140.3% | -444.1% | · | -814.2% | -211.0% | -372.6% | -411.9% | |
| Pretax Margin | -140.3% | -444.1% | · | -814.2% | -211.0% | -372.6% | -411.9% | |
| EBITDA Margin | -114.8% | -454.9% | · | -676.1% | -173.3% | -375.1% | -438.4% | |
| ROA | -44.4% | -49.5% | -26.1% | -40.6% | -23.3% | -16.9% | -26.0% | |
| ROE | 8062.2% | -180.7% | -73.0% | -107.8% | -42.6% | -27.8% | -28.4% | |
| ROIC | -562.0% | -242.1% | · | -98.8% | -39.5% | -26.2% | · |
Liquidity & Solvency 4
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Current Ratio | 0.7 | 2.0 | 2.4 | 1.9 | 2.7 | 5.0 | 5.5 | |
| Quick Ratio | 0.6 | 1.7 | 2.1 | 1.4 | 2.0 | 3.9 | 4.6 | |
| Debt / Equity | -4.3 | · | · | · | · | · | · | |
| Interest Coverage | -8.7 | -12.4 | -10.3 | -23.5 | -254.1 | -449.4 | -1198.6 |
Efficiency 2
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Asset Turnover | 0.3 | 0.1 | · | 0.0 | 0.1 | 0.0 | 0.1 | |
| Receivables Turnover | 43.9 | 6.1 | · | · | · | · | · |
Growth Rates 3
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Revenue YoY | 144.6% | 137.4% | -11.9% | -57.8% | 142.2% | · | · | |
| Revenue CAGR 3Y | 72.3% | -4.1% | -3.4% | · | · | · | · | |
| Revenue CAGR 5Y | 39.2% | · | · | · | · | · | · |
Valuation (TTM) 14
| Metric | Trend | 2025 | 2024 | 2023 | 2022 | 2021 | 2020 | 2019 |
|---|---|---|---|---|---|---|---|---|
| Revenue TTM | $81M | $33M | $14M | $16M | $38M | $16M | $13M | |
| Net Income TTM | $-114M | $-148M | $-84M | $-130M | $-80M | $-58M | $-55M | |
| Market Cap | $645M | $477M | $446M | $316M | $1.06B | $669M | $737M | |
| Enterprise Value | $604M | · | · | · | · | · | · | |
| P/E | -5.6 | -2.9 | -4.7 | -2.3 | -13.2 | -9.8 | · | |
| P/S | 7.9 | 14.3 | 31.9 | 19.9 | 28.1 | 43.0 | 55.4 | |
| P/B | -111.3 | 7.0 | 3.2 | 2.7 | 5.7 | 2.8 | 3.9 | |
| P / Tangible Book | · | 7.1 | 3.3 | 2.7 | 5.8 | 2.8 | · | |
| P / Cash Flow | -13.9 | -4.6 | -4.2 | -4.3 | -100.4 | -10.5 | 36.7 | |
| P / FCF | -12.9 | -4.4 | -3.6 | -2.7 | -18.6 | -7.9 | 66.6 | |
| EV / EBITDA | -6.5 | · | · | · | · | · | · | |
| EV / FCF | -12.0 | · | · | · | · | · | · | |
| EV / Revenue | 7.4 | · | · | · | · | · | · | |
| Earnings Yield | -17.9% | -34.8% | -21.2% | -44.0% | -7.6% | -10.2% | · |
Income Statement 14
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Revenue | $321M | $293.0K | $75M | $410.0K | $4M | $2M | $21M | $11M | $282.0K | $697.0K | $2M | $5M | $4M | $3M | · | $5M | |
| R&D Expense | $58M | $32M | $31M | $33M | $33M | $33M | $24M | $26M | $35M | $34M | $34M | $28M | $20M | $22M | $22M | $17M | |
| SG&A Expense | $12M | $9M | $18M | $14M | $12M | $9M | $17M | $13M | $11M | $13M | $12M | $10M | $12M | $13M | $14M | $11M | |
| Operating Expenses | $77M | $41M | $49M | $46M | $48M | $44M | $53M | $51M | $46M | $47M | $46M | $38M | $32M | $35M | $36M | $28M | |
| Operating Income | $244M | $-41M | $26M | $-46M | $-45M | $-42M | $-31M | $-40M | $-46M | $-47M | $-44M | $-33M | $-29M | $-32M | $-41M | $-23M | |
| Interest Expense | $4M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $2M | |
| Interest Income | $706.0K | $189.0K | $278.0K | $161.0K | $408.0K | $971.0K | $1M | $1M | $827.0K | $1M | $549.0K | $523.0K | $655.0K | $545.0K | $432.0K | $288.0K | |
| Income Tax | $2M | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | · | $0 | |
| Net Income | $161M | $-46M | $15M | $-51M | $-39M | $-40M | $-39M | $-39M | $-49M | $-20M | $20M | $-44M | $-30M | $-30M | $-27M | $-37M | |
| EPS (Basic) | $1.76 | $-0.57 | $0.19 | $-0.62 | $-0.48 | $-0.51 | $-0.49 | $-0.55 | $-0.76 | $-0.32 | $0.40 | $-0.74 | $-0.53 | $-0.62 | $-0.58 | $-0.83 | |
| EPS (Diluted) | $1.71 | $-0.57 | $0.19 | $-0.62 | $-0.48 | $-0.51 | $-0.49 | $-0.55 | $-0.76 | $-0.32 | $0.40 | $-0.74 | $-0.53 | $-0.62 | $-0.58 | $-0.83 | |
| Shares (Basic) | 91,418,527 | 81,300,944 | -160,135,483 | 80,947,703 | 80,585,625 | 79,032,341 | -130,253,088 | 71,633,150 | 64,376,396 | 64,065,895 | -107,027,802 | 59,526,642 | 55,349,534 | 48,638,151 | -88,679,332 | 44,687,635 | |
| Shares (Diluted) | 93,805,296 | 81,300,944 | -160,135,483 | 80,947,703 | 80,585,625 | 79,032,341 | -130,253,088 | 71,633,150 | 64,376,396 | 64,065,895 | -107,027,802 | 59,526,642 | 55,349,534 | 48,638,151 | -88,679,332 | 44,687,635 | |
| EBITDA | $244M | $-38M | · | $-43M | $-42M | $-39M | · | $-40M | $-46M | $-43M | · | $-33M | $-29M | $-29M | · | $-23M |
Balance Sheet 28
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Cash & Equivalents | $143M | $72M | $66M | $15M | $32M | $67M | $104M | $123M | $100M | $119M | $130M | $63M | $93M | $69M | $116M | $115M | |
| Receivables | · | $3M | $3M | $3M | $2M | $734.0K | $707.0K | $3M | $2M | $11M | $10M | $22M | $33M | · | $21M | · | |
| Inventory | · | · | · | · | $314.0K | $607.0K | $385.0K | · | · | · | · | · | · | · | · | · | |
| Prepaid Expense | $4M | $6M | $6M | $7M | $7M | $7M | $7M | $7M | $5M | $5M | $6M | $7M | $8M | $7M | $8M | $10M | |
| Other Current Assets | $27M | $670.0K | $2M | $328.0K | $780.0K | $606.0K | $2M | $713.0K | $660.0K | $932.0K | $1M | $758.0K | $2M | $2M | $2M | $2M | |
| Current Assets | $218M | $96M | $92M | $34M | $47M | $80M | $124M | $139M | $111M | $149M | $160M | $104M | $143M | $121M | $154M | $155M | |
| PP&E (Net) | $100M | $103M | $105M | $108M | $111M | $104M | $103M | $113M | $109M | $111M | $116M | $112M | $114M | $113M | $109M | $94M | |
| PP&E (Gross) | · | · | $158M | · | · | · | $145M | · | · | · | $149M | · | · | · | $130M | · | |
| Accum. Depreciation | · | · | $53M | · | · | · | $42M | · | · | · | $33M | · | · | · | $20M | · | |
| Intangibles | $421.0K | $494.0K | $578.0K | $653.0K | $742.0K | $773.0K | $821.0K | $951.0K | $969.0K | $1M | $1M | $1M | $1M | $1M | $1M | $1M | |
| Other Non-current Assets | $1M | $1M | $1M | $1M | $1M | $1M | $1M | $1M | $1M | $1M | $2M | $1M | $1M | $1M | $1M | $1M | |
| Total Assets | $396M | $245M | $244M | $189M | $199M | $224M | $270M | $299M | $267M | $309M | $327M | $267M | $310M | $288M | $318M | $301M | |
| Accounts Payable | $12M | $17M | $10M | $22M | $26M | $20M | $24M | $30M | $21M | $21M | $16M | $21M | $28M | $30M | $17M | $22M | |
| Accrued Liabilities | $21M | $25M | $33M | $24M | $15M | $24M | $27M | $19M | $17M | $17M | $43M | $28M | $25M | $31M | $40M | $25M | |
| Short-term Debt | · | $25M | $25M | $74M | · | · | · | · | · | · | · | · | · | · | · | · | |
| Current Liabilities | $58M | $176M | $123M | $153M | $53M | $52M | $61M | $59M | $47M | $48M | $67M | $64M | $72M | $81M | $82M | $72M | |
| Capital Leases | $10M | $11M | $11M | $12M | $4M | $4M | $8M | $10M | $11M | $12M | $13M | $14M | $16M | $16M | $17M | $17M | |
| Deferred Tax | · | · | · | · | · | · | · | · | · | · | · | $184.0K | $189.0K | $189.0K | $186.0K | $171.0K | |
| Total Liabilities | $181M | $303M | $250M | $230M | $196M | $191M | $202M | $204M | $187M | $188M | $189M | $175M | $187M | $198M | $200M | $179M | |
| Total Debt | · | $25M | · | $74M | · | · | · | · | · | · | · | · | · | · | · | · | |
| Common Stock | $3.0K | $3.0K | $3.0K | $3.0K | $3.0K | $3.0K | $3.0K | $3.0K | $3.0K | $2.0K | $2.0K | $2.0K | $2.0K | $2.0K | $2.0K | $2.0K | |
| Paid-in Capital | $932M | $820M | $808M | $797M | $791M | $780M | $774M | $763M | $707M | $700M | $694M | $659M | $653M | $587M | $582M | $550M | |
| Retained Earnings | $-702M | $-863M | $-816M | $-831M | $-781M | $-742M | $-702M | $-663M | $-623M | $-575M | $-554M | $-574M | $-530M | $-501M | $-470M | $-443M | |
| Treasury Stock | $18M | $18M | · | · | · | · | · | · | · | · | · | · | · | · | · | · | |
| AOCI | $3M | $3M | $2M | $-6M | $-8M | $-5M | $-4M | $-5M | $-4M | $-3M | $-1M | $7M | $1M | $4M | $6M | $15M | |
| Stockholders' Equity | $216M | $-58M | $-6M | $-41M | $3M | $33M | $68M | $96M | $80M | $122M | $138M | $92M | $124M | $90M | $118M | $123M | |
| Liabilities + Equity | $396M | $245M | $244M | $189M | $199M | $224M | $270M | $299M | $267M | $309M | $327M | $267M | $310M | $288M | $318M | $301M | |
| Shares Outstanding | 94,188,118 | 81,446,126 | 81,120,931 | 80,479,684 | 80,446,284 | 79,418,438 | 78,397,380 | 77,695,418 | 64,684,187 | 64,298,691 | 63,601,015 | 59,597,151 | 59,535,314 | 48,477,209 | 48,477,209 | 44,710,678 |
Cash Flow 11
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| D&A | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $3M | $4M | $3M | $3M | $3M | $2M | $2M | |
| Stock-based Comp | $4M | $4M | $6M | $6M | $6M | $5M | $6M | $6M | $6M | $7M | $7M | $7M | $7M | $6M | $7M | $7M | |
| Other Non-cash | · | $57M | · | · | · | $-5M | · | · | · | $-27M | · | · | · | $-17M | · | · | |
| Operating Cash Flow | $-39M | $18M | $47M | $-12M | $-44M | $-37M | $-23M | $-25M | $-19M | $-37M | $-15M | $-24M | $-29M | $-37M | $-16M | $-21M | |
| CapEx | $332.0K | $2M | $272.0K | $610.0K | $1M | $2M | $1M | $730.0K | $1M | $2M | $3M | $4M | $5M | $9M | $8M | $10M | |
| Investing Cash Flow | $-24M | $-2M | $-1M | $-547.0K | $-761.0K | $-2M | $-1M | $-1M | $-1M | $27M | $51M | $-4M | $-5M | $-9M | $-8M | $-10M | |
| Stock Issued | $114M | $14M | $5M | $0 | $5M | $4M | $4M | $52M | $2M | $2M | $30M | $0 | · | · | · | · | |
| Stock Repurchased | $0 | $18M | · | · | · | · | · | · | · | · | · | · | · | · | · | · | |
| Net Stock Activity | · | $-4M | · | · | · | $4M | · | · | · | $2M | · | · | · | · | · | · | |
| Financing Cash Flow | $134M | $-10M | $5M | $-219.0K | $5M | $2M | $4M | $50M | $2M | $-1M | $28M | $-404.0K | $58M | $-1M | $25M | $73M | |
| Free Cash Flow | · | $16M | · | · | · | $-39M | · | · | · | $-38M | · | · | · | $-46M | · | · |
Profitability 5
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Operating Margin | 76.0% | -13930.7% | · | -11232.0% | -1213.6% | · | · | -367.0% | -16279.8% | -6710.5% | · | -642.0% | -813.1% | -952.6% | · | -473.6% | |
| Net Margin | 50.0% | -15806.5% | · | -12320.2% | -1051.1% | · | · | -360.5% | -17241.1% | -2932.9% | · | -868.1% | -835.6% | -910.7% | · | -774.2% | |
| EBITDA Margin | 76.0% | -12904.1% | · | -10462.4% | -1127.1% | · | · | -367.0% | -16279.8% | -6240.6% | · | -642.0% | -813.1% | -859.9% | · | -473.6% | |
| ROA | 54.0% | -19.8% | · | -20.7% | -16.7% | -15.0% | · | -13.9% | -16.9% | -6.8% | · | -15.6% | -10.5% | -10.5% | · | -12.3% | |
| ROE | 146.9% | 370.1% | · | -183.1% | -93.5% | -51.6% | · | -41.9% | -47.8% | -19.3% | · | -41.3% | -22.3% | -24.1% | · | -24.0% |
Liquidity & Solvency 4
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Current Ratio | 3.8 | 0.5 | · | 0.2 | 0.9 | 1.5 | · | 2.3 | 2.4 | 3.1 | · | 1.6 | 2.0 | 1.5 | · | 2.1 | |
| Quick Ratio | 2.5 | 0.4 | · | 0.1 | 0.6 | 1.3 | · | 2.1 | 2.2 | 2.7 | · | 1.4 | 1.7 | 0.8 | · | 1.6 | |
| Debt / Equity | · | -0.4 | · | -1.8 | · | · | · | · | · | · | · | · | · | · | · | · | |
| Interest Coverage | 69.7 | -14.3 | · | -15.0 | -14.8 | -13.7 | · | -11.9 | -14.1 | -14.4 | · | -9.7 | -8.6 | -10.4 | · | -12.1 |
Efficiency 2
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Asset Turnover | 1.1 | 0.0 | · | 0.0 | 0.0 | · | · | 0.0 | 0.0 | 0.0 | · | 0.0 | 0.0 | 0.0 | · | 0.0 | |
| Receivables Turnover | · | 0.1 | · | 0.1 | 1.9 | · | · | 0.8 | 0.0 | 0.1 | · | 0.5 | 0.2 | · | · | · |
Valuation (TTM) 14
| Metric | Trend | Q2 2026 | Q1 2026 | Q4 2025 | Q3 2025 | Q2 2025 | Q1 2025 | Q4 2024 | Q3 2024 | Q2 2024 | Q1 2024 | Q4 2023 | Q3 2023 | Q2 2023 | Q1 2023 | Q4 2022 | Q3 2022 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Revenue TTM | $326M | $6M | · | · | · | $17M | · | $17M | $10M | $13M | · | $17M | $22M | $25M | · | $28M | |
| Net Income TTM | $25M | $-176M | · | $-169M | $-167M | $-148M | · | $-153M | $-143M | $-125M | · | $-142M | $-131M | $-133M | · | $-128M | |
| Market Cap | $1.27B | $705M | · | $662M | $525M | $538M | · | $324M | $272M | $390M | · | $293M | $400M | $251M | · | $376M | |
| Enterprise Value | · | $659M | · | $722M | · | · | · | · | · | · | · | · | · | · | · | · | |
| P/E | 337.8 | -4.0 | · | -3.8 | -2.8 | -3.2 | · | -1.8 | -1.8 | -2.7 | · | -1.8 | -2.5 | -1.8 | · | -2.9 | |
| P/S | 3.9 | 111.6 | · | · | · | 31.7 | · | 19.1 | 28.3 | 30.8 | · | 17.4 | 17.8 | 10.2 | · | 13.4 | |
| P/B | 5.9 | -12.1 | · | -16.3 | 177.2 | 16.3 | · | 3.4 | 3.4 | 3.2 | · | 3.2 | 3.2 | 2.8 | · | 3.1 | |
| P / Tangible Book | 5.9 | · | · | · | 236.5 | 16.7 | · | 3.4 | 3.4 | 3.2 | · | 3.2 | 3.3 | 2.8 | · | 3.1 | |
| P / Cash Flow | · | 39.6 | · | · | · | -14.6 | · | · | · | -10.6 | · | · | · | -6.7 | · | · | |
| P / FCF | · | 44.6 | · | · | · | -14.0 | · | · | · | -10.2 | · | · | · | -5.4 | · | · | |
| EV / EBITDA | · | -17.4 | · | -16.8 | · | · | · | · | · | · | · | · | · | · | · | · | |
| EV / FCF | · | 41.7 | · | · | · | · | · | · | · | · | · | · | · | · | · | · | |
| EV / Revenue | · | 104.2 | · | · | · | · | · | · | · | · | · | · | · | · | · | · | |
| Earnings Yield | 0.30% | -25.2% | · | -26.2% | -35.3% | -31.6% | · | -56.8% | -55.8% | -36.4% | · | -55.4% | -40.8% | -56.3% | · | -34.2% |
Financial Statements Income statement, balance sheet, cash flow — annual, last 5 years
Income Statement
| 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | |
|---|---|---|---|---|---|
| Revenue | $81M | $33M | $14M | $16M | $38M |
| Operating Margin % | -130.2% | -493.4% | — | -730.9% | -194.1% |
| Net Income | $-114M | $-148M | $-84M | $-130M | $-80M |
| Diluted EPS | $-1.42 | $-2.12 | $-1.49 | $-2.87 | $-1.80 |
Balance Sheet
| 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | |
|---|---|---|---|---|---|
| Debt / Equity | -4.3 | — | — | — | — |
| Current Ratio | 0.7 | 2.0 | 2.4 | 1.9 | 2.7 |
| Quick Ratio | 0.6 | 1.7 | 2.1 | 1.4 | 2.0 |
Cash Flow
| 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | |
|---|---|---|---|---|---|
| Free Cash Flow | $-50M | $-109M | $-126M | $-118M | $-57M |
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Institutional owners (13F) 166 filers · $936.5M total · As of June 30, 2026
Institutions that report holding this stock in their quarterly SEC Form 13F. Long positions only; a single filer may appear twice for separate option legs. Large offsetting put/call legs typically reflect market-making or hedged inventory, not directional conviction.
| New positions | Exited positions | Increased | Decreased | Net shares change |
|---|---|---|---|---|
| 44 (+24 vs prior Q) | 11 (-5 vs prior Q) | 70 (+23 vs prior Q) | 27 (-7 vs prior Q) | +9.2M |
Compared to Q1 2026. SEC Form 13F filings are due within 45 days of quarter-end plus a short buffer for late filers — quarters still inside that window are skipped in favor of the most recent fully-reported pair.
| Institution | Value | Shares | % of tracked 13F | Type |
|---|---|---|---|---|
| Sanofi | $164,791,427 | 12,197,737 | 17.60% | Shares |
| PERCEPTIVE ADVISORS LLC | $145,727,749 | 10,786,658 | 15.56% | Shares |
| Rubric Capital Management LP | $122,941,000 | 9,100,000 | 13.13% | Shares |
| JOHNSON & JOHNSON | $89,720,775 | 6,641,064 | 9.58% | Shares |
| ADAGE CAPITAL PARTNERS GP, L.L.C. | $59,444,000 | 4,400,000 | 6.35% | Shares |
| Opaleye Management Inc. | $47,960,500 | 3,550,000 | 5.12% | Shares |
| MILLENNIUM MANAGEMENT LLC | $40,148,370 | 2,971,752 | 4.29% | Shares |
| 683 Capital Management, LLC | $31,073,000 | 2,300,000 | 3.32% | Shares |
| Woodline Partners LP | $20,266,824 | 1,500,135 | 2.16% | Shares |
| STATE STREET CORP | $18,822,429 | 1,393,222 | 2.01% | Shares |
| Knoll Capital Management, LLC | $16,887,500 | 1,250,000 | 1.80% | Shares |
| KENNEDY CAPITAL MANAGEMENT LLC | $14,934,238 | 1,105,421 | 1.59% | Shares |
| Long Focus Capital Management, LLC | $14,594,853 | 1,080,300 | 1.56% | Shares |
| JACOBS LEVY EQUITY MANAGEMENT, INC | $13,714,082 | 1,015,106 | 1.46% | Shares |
| HEIGHTS CAPITAL MANAGEMENT, INC | $11,483,500 | 850,000 | 1.23% | Shares |
| GEODE CAPITAL MANAGEMENT, LLC | $10,297,497 | 762,213 | 1.10% | Shares |
| VANGUARD PORTFOLIO MANAGEMENT LLC | $9,775,336 | 723,563 | 1.04% | Shares |
| CITADEL ADVISORS LLC | $8,788,106 | 650,489 | 0.94% | Shares |
| Erste Asset Management GmbH | $8,667,648 | 691,200 | 0.93% | Shares |
| J. Goldman & Co LP | $8,132,642 | 601,972 | 0.87% | Shares |
| PFM Health Sciences, LP | $6,150,914 | 455,286 | 0.66% | Shares |
| PANAGORA ASSET MANAGEMENT INC | $4,730,851 | 350,174 | 0.51% | Shares |
| BANK OF AMERICA CORP /DE/ | $2,815,430 | 208,396 | 0.30% | Shares |
| Point72 Asset Management, L.P. | $2,734,329 | 202,393 | 0.29% | Shares |
| Ghisallo Capital Management LLC | $2,702,000 | 200,000 | 0.29% | Shares |
| Privium Fund Management B.V. | $2,649,473 | 196,112 | 0.28% | Shares |
| BlackRock, Inc. | $2,628,343 | 194,548 | 0.28% | Shares |
| AQR CAPITAL MANAGEMENT LLC | $2,552,620 | 188,943 | 0.27% | Shares |
| Squarepoint Ops LLC | $2,194,186 | 162,412 | 0.23% | Shares |
| JPMORGAN CHASE & CO | $2,144,353 | 171,001 | 0.23% | Shares |
| Y-Intercept (Hong Kong) Ltd | $2,000,358 | 148,065 | 0.21% | Shares |
| CHARLES SCHWAB INVESTMENT MANAGEMENT INC | $1,924,283 | 142,434 | 0.21% | Shares |
| BLAIR WILLIAM & CO/IL | $1,695,208 | 125,478 | 0.18% | Shares |
| Voleon Capital Management LP | $1,591,343 | 117,790 | 0.17% | Shares |
| GOLDMAN SACHS GROUP INC | $1,573,861 | 116,496 | 0.17% | Shares |
| Swiss National Bank | $1,505,014 | 111,400 | 0.16% | Shares |
| D. E. Shaw & Co., Inc. | $1,437,599 | 106,410 | 0.15% | Shares |
| BARCLAYS PLC | $1,283,126 | 94,976 | 0.14% | Shares |
| ALPS ADVISORS INC | $1,258,943 | 93,186 | 0.13% | Shares |
| Prosight Management, LP | $1,215,900 | 90,000 | 0.13% | Shares |
| Aquatic Capital Management LLC | $1,176,235 | 87,064 | 0.13% | Shares |
| RHUMBLINE ADVISERS | $1,173,305 | 86,848 | 0.13% | Shares |
| J. Goldman & Co LP | $1,118,628 | 82,800 | 0.12% | Call option |
| TOCQUEVILLE ASSET MANAGEMENT L.P. | $1,049,727 | 77,700 | 0.11% | Shares |
| DAVENPORT & Co LLC | $977,719 | 72,370 | 0.10% | Shares |
| Engineers Gate Manager LP | $933,433 | 69,092 | 0.10% | Shares |
| Fort Sheridan Advisors LLC | $897,611 | 66,441 | 0.10% | Shares |
| Quantinno Capital Management LP | $893,470 | 66,134 | 0.10% | Shares |
| Trexquant Investment LP | $883,459 | 65,393 | 0.09% | Shares |
| AMERIPRISE FINANCIAL INC | $803,413 | 59,468 | 0.09% | Shares |
| AlphaCentric Advisors LLC | $735,876 | 54,469 | 0.08% | Shares |
| WELLS FARGO & COMPANY/MN | $728,311 | 53,909 | 0.08% | Shares |
| VANGUARD FIDUCIARY TRUST CO | $677,689 | 50,162 | 0.07% | Shares |
| BROWN ADVISORY INC | $675,500 | 50,000 | 0.07% | Shares |
| STATE OF WISCONSIN INVESTMENT BOARD | $664,692 | 49,200 | 0.07% | Shares |
| AMH Equity Ltd | $658,400 | 80,000 | 0.07% | Shares |
| SUSQUEHANNA INTERNATIONAL GROUP, LLP | $654,884 | 48,474 | 0.07% | Shares |
| MARTINGALE ASSET MANAGEMENT L P | $646,508 | 47,854 | 0.07% | Shares |
| SEI INVESTMENTS CO | $643,076 | 47,600 | 0.07% | Shares |
| Bank of New York Mellon Corp | $638,564 | 47,266 | 0.07% | Shares |
| WELLINGTON MANAGEMENT GROUP LLP | $611,490 | 45,262 | 0.07% | Shares |
| VANGUARD ASSET MANAGEMENT, Ltd | $544,980 | 40,339 | 0.06% | Shares |
| Zurcher Kantonalbank (Zurich Cantonalbank) | $543,007 | 40,193 | 0.06% | Shares |
| MetLife Investment Management, LLC | $476,606 | 35,278 | 0.05% | Shares |
| ALLIANCEBERNSTEIN L.P. | $473,615 | 54,690 | 0.05% | Shares |
| EntryPoint Capital, LLC | $466,230 | 34,510 | 0.05% | Shares |
| Virtus Investment Advisers, LLC | $460,948 | 34,119 | 0.05% | Shares |
| LETKO, BROSSEAU & ASSOCIATES INC | $432,320 | 32,000 | 0.05% | Shares |
| AXQ CAPITAL, LP | $421,363 | 31,189 | 0.04% | Shares |
| PUBLIC EMPLOYEES RETIREMENT SYSTEM OF OHIO | $414,757 | 30,700 | 0.04% | Shares |
| CITIGROUP INC | $390,223 | 28,884 | 0.04% | Shares |
| TWO SIGMA INVESTMENTS, LP | $388,669 | 28,769 | 0.04% | Shares |
| HSBC HOLDINGS PLC | $379,142 | 28,898 | 0.04% | Shares |
| XTX Topco Ltd | $378,375 | 28,007 | 0.04% | Shares |
| PRUDENTIAL FINANCIAL INC | $378,212 | 27,995 | 0.04% | Shares |
| MIRAE ASSET GLOBAL ETFS HOLDINGS Ltd. | $374,011 | 27,684 | 0.04% | Shares |
| CreativeOne Wealth, LLC | $356,988 | 26,424 | 0.04% | Shares |
| Mitsubishi UFJ Asset Management Co., Ltd. | $331,373 | 24,528 | 0.04% | Shares |
| DIVERSIFIED TRUST CO | $323,186 | 23,922 | 0.03% | Shares |
| Invesco Ltd. | $318,944 | 23,608 | 0.03% | Shares |
| IEQ CAPITAL, LLC | $301,678 | 22,330 | 0.03% | Shares |
| STRS OHIO | $299,922 | 22,200 | 0.03% | Shares |
| NEW YORK STATE COMMON RETIREMENT FUND | $284,561 | 21,063 | 0.03% | Shares |
| State of New Jersey Common Pension Fund D | $242,599 | 17,957 | 0.03% | Shares |
| Police & Firemen's Retirement System of New Jersey | $239,559 | 17,732 | 0.03% | Shares |
| Beacon Pointe Advisors, LLC | $231,768 | 26,763 | 0.02% | Shares |
| MANUFACTURERS LIFE INSURANCE COMPANY, THE | $230,075 | 17,030 | 0.02% | Shares |
| Vanguard Investments Australia, Ltd. | $209,891 | 15,536 | 0.02% | Shares |
| MORGAN STANLEY | $208,081 | 15,402 | 0.02% | Shares |
| ARIZONA STATE RETIREMENT SYSTEM | $207,027 | 15,324 | 0.02% | Shares |
| Entropy Technologies, LP | $204,487 | 15,136 | 0.02% | Shares |
| Perigon Wealth Management, LLC | $203,042 | 15,029 | 0.02% | Shares |
| China Universal Asset Management Co., Ltd. | $199,124 | 14,739 | 0.02% | Shares |
| MERCER GLOBAL ADVISORS INC /ADV | $195,909 | 14,501 | 0.02% | Shares |
| nVerses Capital, LLC | $189,977 | 14,062 | 0.02% | Shares |
| Schonfeld Strategic Advisors LLC | $170,684 | 12,634 | 0.02% | Shares |
| KLP KAPITALFORVALTNING AS | $170,226 | 12,600 | 0.02% | Shares |
| INTECH INVESTMENT MANAGEMENT LLC | $168,834 | 12,497 | 0.02% | Shares |
| STATE BOARD OF ADMINISTRATION OF FLORIDA RETIREMENT SYSTEM | $165,322 | 12,237 | 0.02% | Shares |
| VOYA INVESTMENT MANAGEMENT LLC | $164,890 | 12,205 | 0.02% | Shares |
Company insiders 17 insiders · 7 officers · 10 directors
| Insider | Role | Last activity | Shares owned | Buys 12m | Sells 12m | Net 12m |
|---|---|---|---|---|---|---|
| Alexandria Forbes | PRESIDENT & CEO | Aug. 18, 2026 S | 1,325,695 | 0 | 1 | $-859,320 |
| Richard Giroux | CFO & COO | July 21, 2026 S | 908,530 | 0 | 1 | $-700,560 |
| Katherine Breedis | Chief Financial Officer | Dec. 29, 2018 A | — | 0 | 0 | $0 |
| Stuart Naylor | CHIEF SCI OFCR, OPHTHALMOLOGY | July 7, 2026 S | 640,846 | 0 | 2 | $-409,470 |
| Robert J Wollin | GENERAL COUNSEL AND SECRETARY | June 25, 2026 A | — | 0 | 0 | $0 |
| Robert K Zeldin | CHIEF MEDICAL OFFICER | June 25, 2026 A | — | 0 | 0 | $0 |
| Bruce Gottlieb | General Counsel | April 1, 2019 A | — | 0 | 0 | $0 |
| Debra Yu | Director | June 11, 2026 A | — | 0 | 0 | $0 |
| Ellen Hukkelhoven | Director | June 11, 2026 A | — | 0 | 0 | $0 |
| Keith R. Harris | Director | June 11, 2026 A | 200,000 | 0 | 0 | $0 |
| Neil Mendoza | Director | June 11, 2026 A | — | 0 | 0 | $0 |
| Nicole Seligman | Director | June 11, 2026 A | 5,000 | 0 | 0 | $0 |
| Thomas E Shenk | Director | June 11, 2026 A | 157,476 | 0 | 0 | $0 |
| Martin Indyk | Director | June 10, 2021 A | — | 0 | 0 | $0 |
| Joel S Marcus | Director | June 10, 2021 A | 12,882 | 0 | 0 | $0 |
| Arnold J Levine | Director | June 10, 2021 A | — | 0 | 0 | $0 |
| Johnson & Johnson Innovation - JJDC, Inc. | 10% owner | Sept. 15, 2023 J | 0 | 0 | 0 | $0 |
Insiders from SEC Form 3/4/5 filings; net = open-market P/S only
Activists & 5%+ owners 1 position
Investors who filed SEC Schedule 13D — beneficial ownership above 5% with an intent to influence the issuer (activist stakes, board campaigns, M&A). Each row shows the most recent known state of that filer's position.
| Filer | Filed | Stake | Status | Purpose | Filing |
|---|---|---|---|---|---|
| Perceptive Advisors LLC, Joseph Edelman, Perceptive Life Sciences Master Fund, Ltd. ×9 filings | April 24, 2026 | 12.60% | Amendment | — | SEC |
Purpose is an automated classification of the filer's own stated purpose (SEC Item 4) — not investment advice. "—" means no clear purpose was stated or the text could not be classified.
ETF ownership Held by 19 ETFs
Weight reflects direct equity holdings (N-PORT) only; leveraged or derivative-based funds may hold additional swap exposure not shown.
| Fund | Weight | Units | As of | Source |
|---|---|---|---|---|
| IWC · iShares Trust | 0.18% | 204,349 SH | Aug. 8, 2026 | Daily |
| ESSC · Strategy Shares | 0.11% | 2,988 NS | April 30, 2026 | N-PORT |
| IBBQ · Invesco Exchange-Traded Fund Trust … | 0.08% | 5,038 SH | Aug. 8, 2026 | Daily |
| IBB · iShares Trust | 0.07% | 518,715 SH | Aug. 8, 2026 | Daily |
| VTWG · VANGUARD SCOTTSDALE FUNDS | 0.04% | 51,041 SH | Aug. 8, 2026 | Daily |
| IWO · iShares Trust | 0.04% | 436,258 SH | Aug. 8, 2026 | Daily |
| PRFZ · Invesco Exchange-Traded Fund Trust | 0.03% | 56,977 SH | Aug. 8, 2026 | Daily |
| IWM · iShares Trust | 0.02% | 1,524,242 SH | Aug. 8, 2026 | Daily |
| VTWO · VANGUARD SCOTTSDALE FUNDS | 0.02% | 345,700 SH | Aug. 8, 2026 | Daily |
| ISCG · iShares Trust | 0.02% | 12,859 SH | Aug. 8, 2026 | Daily |
| RSSL · Global X Funds | 0.01% | 19,896 NS | April 30, 2026 | N-PORT |
| VTWV · VANGUARD SCOTTSDALE FUNDS | 0.01% | 11,041 SH | Aug. 8, 2026 | Daily |
| IWN · iShares Trust | 0.01% | 113,223 SH | Aug. 8, 2026 | Daily |
| VHT · VANGUARD WORLD FUND | 0.01% | 167,269 SH | Aug. 8, 2026 | Daily |
| ISCB · iShares Trust | 0.01% | 1,898 SH | Aug. 8, 2026 | Daily |
| WSML · iShares Trust | 0.01% | 3,405 SH | Aug. 8, 2026 | Daily |
| MSSM · MORGAN STANLEY PATHWAY FUNDS | 0.00% | 1,432 NS | May 31, 2026 | N-PORT |
| IWV · iShares Trust | 0.00% | 17,435 SH | Aug. 8, 2026 | Daily |
| VTHR · VANGUARD SCOTTSDALE FUNDS | 0.00% | 5,601 SH | Aug. 8, 2026 | Daily |